UK approves gene therapy to cure two blood disorders - BBC News
7 months ago
5
In a world first, medical regulators in the UK have approved a gene therapy that aims to cure sickle cell disease and beta thalassemia.
The treatment is the first to be licensed using the gene-editing tool known as Crispr, for which its discoverers were awarded the Nobel prize in 2020.
It is a revolutionary advance for two inherited blood conditions, both triggered by errors in the gene for haemoglobin.
In trials, 28 out of 29 sickle cell patients were free of severe pain and 39 of 42 beta thalassemia patients no longer needed blood transfusions for at least a year.
The trials are continuing in the UK, US, France, Germany and Italy.
Loading comments...
-
2:17:00
Fed Reacts
6 hours agoFed Explains Foolio Shot After Celebrating Birthday
13.5K13 -
3:54:46
Due Dissidence
1 day agoBowman, AOC, Bernie a BUST at Bronx Rally, Jose Vega DENIED Entry, Teamsters Prez to SPEAK at RNC
31.3K36 -
LIVE
SonnyFaz
9 hours agoSONNY X SHANNEY RICH
1,917 watching -
2:40:17
vivafrei
13 hours agoEp. 216: SCOTUS RULINGS GALORE! Kansas Sues Pfizer! Trump Gag Order! Recusal of Nipple Judge? & MORE
123K223 -
19:28
Stephen Gardner
3 days ago🔴BREAKING: Biden’s RECKLESS new scheme fails with the PEOPLE!!
100K169 -
LIVE
Vigilant News Network
11 hours agoMedia Blackout: 10 News Stories They Chose Not to Tell You - Episode 28
2,027 watching -
13:07
Evenout
11 hours agoStealing Jordan 1 OG Then Re-Appearing With a Different Shoes Twin Prank!
50.8K9 -
1:20:26
Winston Marshall
1 day agoUNCOVERED: Legal System Weaponised - Trump, Hunter, Bannon & Biden | The Winston Marshall Show #020
90.5K157 -
16:09
Chicks in the Office
13 hours agoOur Top 12 Songs On Repeat This Week - Music You Can't Miss
79.4K37 -
2:23:05
Gigi Young
2 days agoLecture: The Mystery of Death
73.3K4